View source for PYC Therapeutics Limited (20250002917). METHOD OF TREATMENT FOR OPTIC ATROPHY

=METHOD OF TREATMENT FOR OPTIC ATROPHY=


==Organization Name==

[[:Category:PYC Therapeutics Limited|PYC Therapeutics Limited]]


[[Category:PYC Therapeutics Limited]]

==Inventor(s)==

[[:Category:Janya Grainok of Nedlands AU|Janya Grainok of Nedlands AU]][[Category:Janya Grainok of Nedlands AU]]

[[:Category:Kim Rice of Nedlands AU|Kim Rice of Nedlands AU]][[Category:Kim Rice of Nedlands AU]]

[[:Category:Sasiwimon Utama of Nedlands AU|Sasiwimon Utama of Nedlands AU]][[Category:Sasiwimon Utama of Nedlands AU]]

==METHOD OF TREATMENT FOR OPTIC ATROPHY==


This abstract first appeared for US patent application 20250002917 titled 'METHOD OF TREATMENT FOR OPTIC ATROPHY

==Original Abstract Submitted==

the present invention relates to isolated or purified antisense oligonucleotides that bind to intron 7 of an opa1 gene pre-mrna. the present invention also relates to methods of manipulating translation of the opa1 gene transcript and use of the antisense oligonucleotide to treat. prevent or ameliorate the effects caused by mutations in the gene opa1.



[[Category:C12N15/113]]
[[Category:A61P27/02]]
[[Category:CPC_C12N15/113]]