PYC Therapeutics Limited (20250002917). METHOD OF TREATMENT FOR OPTIC ATROPHY
METHOD OF TREATMENT FOR OPTIC ATROPHY
Organization Name
Inventor(s)
Sasiwimon Utama of Nedlands AU
METHOD OF TREATMENT FOR OPTIC ATROPHY
This abstract first appeared for US patent application 20250002917 titled 'METHOD OF TREATMENT FOR OPTIC ATROPHY
Original Abstract Submitted
the present invention relates to isolated or purified antisense oligonucleotides that bind to intron 7 of an opa1 gene pre-mrna. the present invention also relates to methods of manipulating translation of the opa1 gene transcript and use of the antisense oligonucleotide to treat. prevent or ameliorate the effects caused by mutations in the gene opa1.