Precision BioSciences, Inc. (20250152679). DYSTROPHIN GENE EXON DELETION USING ENGINEERED NUCLEASES
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DYSTROPHIN GENE EXON DELETION USING ENGINEERED NUCLEASES
Abstract: the invention relates to the field of molecular biology and recombinant nucleic acid technology. in particular, the invention relates to a method of treating a patient with duchenne muscular dystrophy comprising the removal of at least one exon from the dystrophin gene using engineered nucleases.
IPC:
CPC: A61K38/465,