METHODS OF TREATING NEURODEGENERATIVE DISORDERS

Abstract: provided herein are expression cassettes for expressing a transgene in a cell, wherein the transgene encodes a disorder-related polypeptide. also provided are methods to treat various neurodegenerative disorders. further provided herein are vectors (e.g., raav vectors), viral particles, pharmaceutical compositions and kits for expressing a disorder-related polypeptide in an individual in need thereof.

IPC:

CPC: A61K48/0058,