METHODS OF TREATING NEURODEGENERATIVE DISORDERS

Abstract: provided herein are expression cassettes for expressing a transgene in a cell, wherein the transgene encodes a disorder-related polypeptide. also provided are methods to treat various neurodegenerative disorders. further provided herein are vectors (e.g., raav vectors), viral particles, pharmaceutical compositions and kits for expressing a disorder-related polypeptide in an individual in need thereof.

Inventor(s): Shyam RAMACHANDRAN

CPC Classification: A61K48/0058 (Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy)

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