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Category:C12N15/113
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Pages in category "C12N15/113"
The following 126 pages are in this category, out of 126 total.
1
- 18007439. GENE CORRECTION FOR SCID-X1 IN LONG-TERM HEMATOPOIETIC STEM CELLS simplified abstract (THE BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY)
- 18187102. Compositions and methods for improved malonyl-CoA biosynthesis using 2-stage dynamic metabolic control simplified abstract (Duke University)
- 18248988. NOVEL LIGANDS FOR ASIALOGLYCOPROTEIN RECEPTOR simplified abstract (SANOFI)
- 18251227. SIRNA-NANOBOWL-MEDIATED INTERVENTION OF COVID-19 simplified abstract (THE REGENTS OF THE UNIVERSITY OF CALIFORNIA)
- 18270014. Suppression-Replacement Gene Therapy simplified abstract (Mayo Foundation for Medical Education and Research)
- 18273716. METHODS FOR TREATING AND AMELIORATING CANCER simplified abstract (THE REGENTS OF THE UNIVERSITY OF CALIFORNIA)
- 18274133. PHOTO-CROSSLINKED BIOREDUCIBLE POLYMERIC NANOPARTICLES FOR ENHANCED RNA DELIVERY (The Johns Hopkins University)
- 18280126. METHODS OF MODULATING NEURONAL AND OLIGODENDROCYTE SURVIVAL simplified abstract (THE BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY)
- 18286984. PROMOTERS FOR VIRAL-BASED GENE THERAPY (The Regents of the University of California)
- 18289921. METHODS AND COMPOSITIONS FOR TREATING EPILEPSY (CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE)
- 18323956. REPROGRAMMING OF NON-NEURONAL CELLS INTO NEURONS AND METHODS AND COMPOSITIONS TO TREAT NEURODEGENERATIVE DISEASES AND DISORDERS simplified abstract (THE REGENTS OF THE UNIVERSITY OF CALIFORNIA)
- 18402154. SPLICE-SWITCHING OLIGONUCLEOTIDES AND METHODS OF USE simplified abstract (Duke University)
- 18421326. Treatment Of Stroke With 1,4-Alpha-Glucan-Branching Enzyme (GBE1) Inhibitors simplified abstract (Regeneron Pharmaceuticals, Inc.)
- 18449940. DEAD GUIDES FOR CRISPR TRANSCRIPTION FACTORS simplified abstract (Massachusetts Institute of Technology)
- 18463589. TARGETED NON-VIRAL DNA INSERTIONS simplified abstract (The Regents of the University of California)
- 18487429. SOLUBLE INTERLEUKIN-7 RECEPTOR (SIL7R) MODULATING THERAPY TO TREAT AUTOIMMUNE DISEASES AND CANCER simplified abstract (Board of Regents, The University of Texas System)
- 18501859. Methods and Compositions for Treating, Ameliorating, and/or Preventing Chronic Kidney Disease (CKD) and Complications thereof by Regulating DPEP1, CASP9, ACSS2 and/or FASN simplified abstract (The Trustees of the University of Pennsylvania)
- 18503125. SOLUBLE INTERLEUKIN-7 RECEPTOR (SIL7R) MODULATING THERAPY TO TREAT AUTOIMMUNE DISEASES AND CANCER simplified abstract (Board of Regents, The University of Texas System)
- 18544247. GENE THERAPY TREATMENT OF ATRIAL FIBRILLATION simplified abstract (NORTHWESTERN UNIVERSITY)
- 18559667. PRODUCTION OF THERAPEUTIC MESENCHYMAL STEM CELL-DERIVED EXOSOMES simplified abstract (BOARD OF REGENTS, THE UNIVERSITY OF TEXAS SYSTEM)
- 18575450. TARGETING PIEZO1 TO TREAT INHERITED AND AGE-RELATED MACULAR DEGENERATIONS simplified abstract (The Regents of the University of California)
- 18577881. METHODS OF CONTROLLING RNA BINDING PROTEIN ACTIVITY simplified abstract (The Regents of the University of California)
- 18602410. IMMOLATIVE CELL-PENETRATING COMPLEXES FOR NUCLEIC ACID DELIVERY simplified abstract (The Board of Trustees of the Leland Stanford Junior University)
- 18608561. METHODS AND COMPOSITIONS FOR SENSITIZATION OF TUMOR CELLS TO IMMUNE THERAPY simplified abstract (Regeneron Pharmaceuticals, Inc.)
- 18618604. RNA EDITING simplified abstract (HOFFMANN-LA ROCHE INC.)
- 18659737. COMPOSITIONS AND METHODS FOR CORRECTING LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2C USING EXON SKIPPING simplified abstract (Northwestern University)
- 18668366. MICROPEPTIDES AND USE OF SAME FOR MODULATING GENE EXPRESSION simplified abstract (CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE)
- 18675023. OLIGONUCLEOTIDES FOR TISSUE SPECIFIC GENE EXPRESSION MODULATION (University of Massachusetts)
- 18684960. PEPTIDE-BINDING HYBRID LIPOSOME EXOSOME, PEPTIDE-BINDING EXOSOME, COMPOSITION CONTAINING SAME, AND METHOD OF FORMING SAME (SEKISUI CHEMICAL CO., LTD.)
- 18688144. DELIVERY OF ANITSENSE OLIGOMERS BY MIRROR IMAGE PEPTIDES (Massachusetts Institute of Technology)
- 18709695. IRAP INHIBITORS FOR USE IN THE TREATMENT OF INFLAMMATORY DISEASES (CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE)
- 18725289. IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING (Massachusetts Institute of Technology)
- 18735668. ANTISENSE OLIGONUCLEOTIDES TARGETING ACTL6B simplified abstract (Hoffmann-La Roche Inc.)
- 18742639. ORAL CODELIVERY OF 5-FLUOREURACIL AND Bcl2 siRNA TREATING STOMACH CANCER (Board of Regents, The University of Texas System)
- 18742746. ORAL CODELIVERY OF NAVITOCLAX AND Bcl2 siRNA TREATING GASTIC CANCER (Board of Regents, The University of Texas System)
- 18744136. TIS-L TARGETING ANTIVIRAL ANTISENSE OLIGONUCLEOTIDE WITH ABILITY TO INHIBIT VIRAL REPLICATION OF SARS-COV-2 (KOREA ADVANCED INSTITUTE OF SCIENCE AND TECHNOLOGY)
- 18749156. THREOSE NUCLEIC ACID ANTISENSE OLIGONUCLEOTIDES AND METHODS THEREOF simplified abstract (HOFFMANN-LA ROCHE INC.)
- 18751096. THERAPEUTIC TREATMENT FOR FRAGILE X-ASSOCIATED DISORDER (University of Massachusetts)
- 18751730. Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription (THE REGENTS OF THE UNIVERSITY OF CALIFORNIA)
- 18764835. Compositions and Methods for Modulating Single Stranded DNA Regions that Catalyze Enzymatic Reactions (The Trustees of the University of Pennsylvania)
- 18782680. METHODS OF MODULATING RNA TRANSLATION (THE REGENTS OF THE UNIVERSITY OF CALIFORNIA)
- 18885092. COMPOUND AND LIPID COMPOSITION (FUJIFILM Corporation)
- 18907274. COMPOSITIONS AND METHODS USEFUL IN PROMOTING MILK PRODUCTION (The Regents of the University of California)
- 18942238. METHODS FOR THE TREATMENT OF NLRP3 RELATED DISORDERS (THE REGENTS OF THE UNIVERSITY OF CALIFORNIA)
- 18956207. RIBOZYME-ASSISTED CIRCULAR RNAS AND COMPOSITIONS AND METHODS OF USE THEREOF (MASSACHUSETTS INSTITUTE OF TECHNOLOGY)
- 18962390. SYSTEMS, METHODS, AND COMPOSITIONS FOR SITE-SPECIFIC GENETIC ENGINEERING USING PROGRAMMABLE ADDITION VIA SITE-SPECIFIC TARGETING ELEMENTS (PASTE) (MASSACHUSETTS INSTITUTE OF TECHNOLOGY)
2
A
- AMGEN INC. (20250011779). COMPOSITIONS AND METHODS FOR ENHANCING GENE SILENCING ACTIVITY OF OLIGONUCLEOTIDE COMPOUNDS
- Arrowhead Pharmaceuticals, Inc. (20250092072). Trialkyne Linking Agents and Methods of Use
- AstraZeneca Ireland Limited (20250002908). COMPOSITIONS AND METHODS FOR INHIBITING COMPLEMENT COMPONENT 3 EXPRESSION
B
- Biotechnology patent applications on 21st Mar 2025
- Biotechnology patent applications on 7th Mar 2025
- Biotechnology patent applications on January 2nd, 2025
- Biotechnology patent applications on June 27th, 2024
- Biotechnology patent applications on March 20th, 2025
- Biotechnology patent applications on March 6th, 2025
- Biotechnology patent applications on May 30th, 2024
- Biotechnology patent applications on November 14th, 2024
- Biotechnology patent applications on September 5th, 2024
- Blockchain patent applications on April 11th, 2024
- Blockchain patent applications on April 4th, 2024
- Blockchain patent applications on February 1st, 2024
- Blockchain patent applications on February 29th, 2024
- Blockchain patent applications on January 25th, 2024
- Blockchain patent applications on March 28th, 2024
- BRCA1 patent applications on January 16th, 2025
C
- Celex Oncology Innovations Limited (20250092399). GENE THERAPY TARGETING THE NEONATAL FORM OF NAV1.5 FOR TREATING CANCER
- CHARLES RIVER LABORATORIES, INC. (20240294943). METHOD FOR IMPROVING GENETIC ENGINEERING OF ADOPTIVE CELL THERAPIES simplified abstract
- CHINESE PLA GENERAL HOSPITAL (20250002911). Engineered Exosome for Treating Hypertrophic Scar (Hts), and Preparation Method and Use Thereof
D
- DNA Storage patent applications on 14th Feb 2025
- DNA Storage patent applications on 14th Mar 2025
- DNA Storage patent applications on 21st Feb 2025
- DNA Storage patent applications on 21st Mar 2025
- DNA Storage patent applications on 28th Feb 2025
- DNA Storage patent applications on February 13th, 2025
- DNA Storage patent applications on February 20th, 2025
- DNA Storage patent applications on February 27th, 2025
- DNA Storage patent applications on February 6th, 2025
- DNA Storage patent applications on January 16th, 2025
- DNA Storage patent applications on January 23rd, 2025
- DNA Storage patent applications on January 2nd, 2025
- DNA Storage patent applications on January 30th, 2025
- DNA Storage patent applications on January 9th, 2025
- DNA Storage patent applications on March 13th, 2025
- DNA Storage patent applications on March 20th, 2025
- Dyne Therapeutics, Inc. (20250066495). MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MUSCULAR DYSTROPHY
- Dyne Therapeutics, Inc. (20250066496). MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
F
I
S
- SAREPTA THERAPEUTICS, INC. (20250011777). DELIVERY OF ANITSENSE OLIGOMERS BY MIRROR IMAGE PEPTIDES
- Secarna Pharmaceuticals GmbH & Co. KG (20250059547). NLRP3 oligonucleotide for use in preventing and/or treating an inflammatory disease
- SHANDONG UNIVERSITY (20250019707). ANTISENSE OLIGONUCLEOTIDE FOR REGULATING BCL2L12 EXPRESSION AND THE USE THEREOF IN TREATMENT OF DISEASES
- Sumitomo Pharma Co., Ltd. (20250084411). Antisense Nucleic Acid
- SynerK Biotech Limited (20240376476). NUCLEIC ACID TARGETING PROPROTEIN CONVERTASE SUBTILISIN/KEXIN 9 AND USES THEREOF simplified abstract
T
- The regents of the university of california (20240336918). METHODS OF CONTROLLING RNA BINDING PROTEIN ACTIVITY simplified abstract
- The regents of the university of california (20250002920). GENETIC MODIFICATION OF MAMMALIAN CELLS TO CONFER RESISTANCE TO CSF1R ANTAGONISTS
- The regents of the university of california (20250064808). METHODS FOR THE TREATMENT OF NLRP3 RELATED DISORDERS
- The regents of the university of california (20250092129). COMPOSITIONS AND METHODS USEFUL IN PROMOTING MILK PRODUCTION
- The regents of the university of california (20250092391). PROMOTERS FOR VIRAL-BASED GENE THERAPY
- THE REGENTS OF THE UNIVERSITY OF CALIFORNIA patent applications on February 27th, 2025
- The Regents of the University of California patent applications on January 2nd, 2025
- The Regents of the University of California patent applications on March 20th, 2025
- The Regents of the University of California patent applications on October 10th, 2024
- The Trustees of Columbia University in the City of New York (20240294643). COMPOSITIONS AND METHODS FOR MODULATING CANCER IMMUNE FITNESS simplified abstract
- THIRD INSTITUTE OF OCEANOGRAPHY, MNR (20250092161). PROMOTION SYSTEM FOR CELLULAR PROTEIN SYNTHESIS AND USE THEREOF
U
- University Of Cincinnati (20250002915). MOLECULAR THERAPEUTICS FOR THE TREATMENT OF HYPERTROPHIC CARDIOMYOPATHY AND HEART FAILURE ASSOCIATED WITH MYBPC3 GENE MUTATIONS
- UNIVERSITY OF MASSACHUSETTS (20240209376). Specific Oligonucleotide-Programmed Readthrough of Nonsense Codons simplified abstract
- University of Massachusetts (20250066780). OLIGONUCLEOTIDES WITH INTERNUCLEOTIDE LINKAGE MODIFICATIONS FOR KIDNEY TARGETING
- University of Rochester (20250019702). GATA4-TARGETED THERAPEUTICS FOR TREATMENT OF CARDIAC HYPERTROPHY
- Unknown Organization (20250019709). NOVEL OXO-RNA COMPOSITIONS AND THE RELATED APPLICATIONS THEREOF
- US Patent Application 18334046. TYPE VI CRISPR ORTHOLOGS AND SYSTEMS simplified abstract
V
- VIB VZW (20240294931). Means and Methods for Improved Regeneration simplified abstract
- VIB VZW (20250011793). Oligonucleotides for Modulating Synaptogyrin-3 Expression
- VICO Therapeutics B.V. (20250011784). RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF NEUROMUSCULAR DISORDERS